Gene therapy is a medical treatment that works by changing or fixing a person's genes to treat or prevent disease ...
Sickle cell disease (SCD) is a group of inherited blood disorders resulting from a mutation in the hemoglobin protein in red blood cells. This mutation changes the shape of the blood cells from round, ...
Screening children for certain clotting proteins may help clinicians in resource-poor settings identify serious complications ...
Two Pee Dee siblings are officially cured of sickle cell disease after more than a decade of living with the genetic blood ...
Serenity Cole enjoyed Christmas last month relaxing with her family near her St. Louis home, making crafts and visiting friends. It was a contrast to how Cole, 18, spent part of the 2024 holiday ...
Sickle Cell Disease (SCD) is a global health challenge that affects millions of people worldwide. Despite significant ...
Vertex Pharmaceuticals and bluebird bio have entered into an agreement with CMS to participate in a new Medicaid payment model for gene-based sickle cell anemia treatments, the agency announced ...