Agence France-Presse

Dubai’s Medcare Hospital Becomes the World’s First to Treat an Adult Spinal Muscular Atrophy (SMA) Patient Outside the US

A multidisciplinary team at Medcare delivered the therapy, led by its Gene Therapy Unit clinical lead, Dr. Vivek Mundada, ...
AsiaOne

'A chance we once only dreamed of': Baby with rare genetic disorder successfully receives $2.4m treatment

After successfully raising the $2.4 million needed to save their child from a rare genetic disorder, baby Faziq finally ...
Healio

Spinal muscular atrophy therapy leads to sustained motor function improvement

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The American Journal of Managed Care

Bridging the Gap: Addressing Unmet Needs in Spinal Muscular Atrophy for Older Patients

Panelists discuss how the current spinal muscular atrophy (SMA) treatment landscape includes 3 options: gene therapy (onasemnogene abeparvovec [Zolgensma]) for younger patients and 2 splice modifiers ...
Forbes

New Gene Therapy Possible For Infants With Spinal Muscular Atrophy

Forbes contributors publish independent expert analyses and insights. Spinal muscular atrophy affects the nerves that control muscle movement, leading to progressive weakening. As a result, infants ...

Student with Disability Dreamed of Bama Rush, but Worried She Didn't Fit the Sorority Girl 'Stereotype.' Inside Her Bid Day Journey (Exclusive)

Ellie Kerrigan, who has spinal muscular atrophy, shared her journey through Alabama sorority recruitment on TikTok ...
ZAWYA

Dubai’s Medcare Hospital becomes world’s first to treat adult Spinal Muscular Atrophy (SMA) patient outside the US

Dubai’s Medcare Hospital becomes world’s first to treat adult Spinal Muscular Atrophy (SMA) patient outside the US ...

Jesy Nelson reveals emotional breakthrough with twin daughter despite condition

'My life is complete.’ ...